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07/01/2025
Challenges in multinational rare disease clinical studies during COVID-19: regulatory assessment of cipaglucosidase alfa plus miglustat in adults with late-onset Pompe disease
Schoser, B, Attarian, S, Graham, R, Holdbrook, F, Goldman, M, Díaz-Manera, J. Challenges in multinational rare disease clinical studies during COVID-19: regulatory assessment of cipaglucosidase alfa plus miglustat in adults with late-onset Pompe disease. JOURNAL OF NEUROLOGY. 2025; 272(1)DOI:10.1007/s00415-024-12843-x. PMID:39775064. IF:4.600(Q1/2D).
01/07/2025
Association of Plasma Phosphorylated Tau 217 With Clinical Deterioration Across Alzheimer Disease Stages.
Selma-Gonzalez J, Rubio-Guerra S, García-Castro J, Vera-Campuzano E, Sala I, Sánchez-Saudinós MB, Zhu N, Arranz J, Arriola-Infante JE, Rodríguez-Baz Í, Maure-Blesa L, Dols-Icardo O, Videla L, Valldeneu S, Barroeta I, Santos-Santos M, Carmona-Iragui M, Vaqué-Alcázar L, Alvarez-Sanchez E, Lorente O, Carreras M, Belbin O, Arslan B, Ashton NJ, Zetterberg H, Blennow K, Montoliu-Gaya L, Bejanin A, Lleó A, Fortea J, Alcolea D, Illan-Gala I. Association of Plasma Phosphorylated Tau 217 With Clinical Deterioration Across Alzheimer Disease Stages.. NEUROLOGY. 2025; 105(1)DOI:10.1212/WNL.0000000000213769. PMID:40472304. IF:(Q/D).
04/01/2024
Severe sperm DNA fragmentation may persist for up to 3 years after cytotoxic therapy in patients affected by Hodgkin lymphoma and non-Hodgkin lymphoma
Farnetani, G, Vannucci, M, Fino, MG, Cioppi, F, Rosta, V, Palma, M, Tamburrino, L, Vinci, S, Casamonti, E, Degl'Innocenti, S, Spinelli, M, Abrardo, C, Marchiani, S, Lotti, F, Muratori, M, Riera-Escamilla, A, Krausz, C. Severe sperm DNA fragmentation may persist for up to 3 years after cytotoxic therapy in patients affected by Hodgkin lymphoma and non-Hodgkin lymphoma. HUMAN REPRODUCTION. 2024; 39(3)DOI:10.1093/humrep/dead269. PMID:38177083. IF:6.100(Q1/1D).
12/10/2023
Frequency, morbidity and equity - the case for increased research on male fertility
Kimmins, S, Anderson, RA, Barratt, CLR, Behre, HM, Catford, SR, De Jonge, CJ, Delbes, G, Eisenberg, ML, Garrido, N, Houston, BJ, Jorgensen, N, Krausz, C, Lismer, A, Mclachlan, RI, Minhas, S, Moss, T, Pacey, A, Priskorn, L, Schlatt, S, Trasler, J, Trasande, L, Tüttelmann, F, Vazquez-Levin, MH, Veltman, JA, Zhang, F, O'Bryan, MK. Frequency, morbidity and equity - the case for increased research on male fertility. Nature Reviews Urology. 2023; DOI:10.1038/s41585-023-00820-4. PMID:37828407. IF:12.100(Q1/1D).